Visionary Ball Seed Grants Scientific Progress Report


Pediatric Brain Injury
Acute Pathophysiological Monitoring and Long-Term Functional Outcome after Pediatric Traumatic Brain Injury
Principal Investigator: Christopher C. Giza, M.D.

This study is unique in that it will correlate child brain injury patients’ detailed acute neuroimaging outcomes, which will be followed over time as the individuals mature. Although the majority of TBI (traumatic brain injury) occurs in the pediatric and young adult age ranges, there has been very limited study with regard to age-dependent mechanisms of injury and recovery. Children are not little adults. Their brain injuries are different, and treating them requires a different approach.

Our first step to this end was to comprehensively characterize the injury types, physiology, treatment and recovery in all children and young adults and look for age-dependent patterns. A further comprehensive analysis is required to map and better understand the trajectory of recovery and how it differs in patients with good recovery vs. bad.

Brain Injury
A Novel Treatment for Human Traumatic Brain Injury: Infusion of Lactate
Principal Investigator: Thomas C. Glenn, Ph.D.

Recently, the UCLA Brain Injury Research Center discovered that the injured brain changes its preference for fuel to help it recover. Consequently, this study aims to determine how the infusion of sodium lactate would affect the brain and systemic physiology in patients with severe traumatic brain injury. Contrary to widely accepted medical practice that regards sodium lactate as an inhibitor to brain recovery, our work has shown that treating TBI patients with sodium lactate infusions decreases their blood acidity, increases blood flow and increases brain energy production.

The next step we take will include studying the effects of varying sodium lactate levels on patient outcome and recovery. Our research may show that these lactate infusions are a crucial differentiator in successful brain repair.

Effect of Traumatic Brain Injury of Subventricular Zone Stem Cell Proliferation
Principal Investigator: Neil G. Harris, Ph.D.

It is now known that the adult brain can generate new cells. Consequently, it is important to determine if these newly born cells could play a role in recovery following traumatic brain injury. Through this grant, we developed an experimental design for determining the fate of cells born within an area of the brain called the subventricular zone following injury. These studies also will determine the role these newly born cells play in recovery of function. Given that there is an endogenous source of new cells, this program will address possible ways to intervene in order to enhance recovery. The first step in or intervention is to determine if the brain grows new cells in response to injury. It may be the case that injury retards the ability of cells to be born, or it may hasten their growth and mobility.

Vagal Nerve Stimulation and Cerebral Glucose Metabolism
Principal Investigator: Richard L. Sutton, Ph.D.

Our objective with this research was to explore the potential mechanisms by which intermittent, low-level stimulation of the vagus nerve stimulation (VNS) improves recovery after experimental traumatic brain injury (TBI). VNS is already approved for human use in the treatment of epilepsy and depression, but heretofore it had not been used to treat human TBI.

Considering how the brain’s glucose metabolism reflects brain activity, our results indicate that VNS treatment may improve behavioral recovery after TBI. Further research demonstrating benefits of this treatment should eventually lead us to clinical trials.

Boosting the Effects of Exercise During the Acute Phase of TBI
Principal Investigator: Fernando Gómez-Pinilla, Ph.D.

Myelin is a protein in the human brain that can be a major obstacle for neuron regeneration after brain injury. Our studies thus far have shown that voluntary exercise following traumatic brain injury (TBI) enabled the body to overcome its own production of two distinct myelin proteins and allow for neural repair. Exercise creates a cellular environment in the brain that is conducive to repair after TBI.

The bigger picture from our findings is exercise’s potential to elevate the injured brain’s capacity for plasticity and repair. Our forthcoming studies will be devoted to using other experimental manipulations to increase the effects of exercise after TBI.

Brain Tumors
Characterization of FOXM1 in Brain Tumor Stem Cells
Principal Investigator: Ichiro Nakano, M.D.

With this grant, our researchers sought to determine whether or not inhibiting FOXM1, a transcription factor that plays a critical role in the formation of cancers, will block the proliferation of stem cells in malignant brain tumors. Our studies have shown that blocking the FOXM1 function resulted in reduced growth of brain tumor cells derived from brain tumor stem cells (BTSC) in culture. Preliminary data suggest that FOXM1 is likely a critical regulator of BTSC survival and/or proliferation.

We have obtained encouraging findings with regard to the effects of inhibition of FOXM1 on BTSC. Throughout the project, we will further characterize the mechanism of the FOXM1 action and the effects of siomycin treatment in malignant brain tumors.

Imaging and Tracking of Interactions Between Tumor-Specific CD8+ T Cells and Brain Tumors In Vivo
Principal Investigator: Robert Prins, Ph.D.

Among the various strategies to treat cancer, immunotherapy may offer us the possibility to counteract tumors with very few negative effects. Until now, immune-based therapies for brain tumors have traditionally lagged behind those for peripheral tumors.
Our research project will hopefully help us to better understand the trafficking patterns of tumor-specific T cells, as well as to validate imaging methods that may be used to determine the efficacy of immune-based protocols for brain tumor therapy. During the next year, we plan to continue these studies and expand the imaging component.

Cognitive Neurophysiology
Single Neuron Studies of Declarative Memory in Humans
Principal Investigator: Itzhak Fried, M.D.

The Cognitive Neurophysiology Laboratory, under the direction of Dr. Itzhak Fried, is studying the function of brain cells in various forms of cognition, including visual perception and memory, auditory function, navigation and motor function. They use a surgical opportunity to directly record individual brain cells as they fire, using depth electrode probes that are implanted in deep areas of the brain in epilepsy patients who are being evaluated for the location of their seizures, so that they can have surgery to cure their epilepsy.

The UCLA depth electrode team is celebrating the 400th patient to undergo depth electrode implantation in more than 35 years of endeavor. The group is recognized worldwide as a leader both in developing novel clinical approaches to surgery for patients with intractable epilepsy and in conducting basic research based on single brain cell recordings.

Brain Monitoring and Modeling
Rule Generation from Clinical Data: A Pilot Study Using BIRC Database and Cardio-Respiratory Arrest Database
Principal Investigator: Valeriy Nenov, Ph.D., Ph.D.

An automated clinical data integration and processing system was developed to derive human-understandable rules for predicting in-hospital acute patient deterioration toward severe cardiac arrest or unplanned ICU transfer. In collaborating with the UCLA Medical Center Quality Management Service, we used the system to analyze historical cases of cardiac arrests and unplanned ICU transfers that were logged in the calendar years 2005 and 2006. Positive results regarding the predictive power of the derived rules were established. We are working on a further improvement of the system for integrating continuous physiological signals into the system.